UCEDD
University Center for Excellence in Developmental Disabilities

Single-dose, subcutaneous recombinant phenylalanine ammonia lyase conjugated with polyethylene glycol in adult patients with phenylketonuria: an open-label, multicentre, phase 1 dose-escalation trial

, V. Single-Dose, Subcutaneous Recombinant Phenylalanine Ammonia Lyase Conjugated With Polyethylene Glycol in Adult Patients With Phenylketonuria: An Open-Label, Multicentre, Phase 1 Dose-Escalation Trial.

Longo N, Harding CO, Burton BK, Grange DK, Vockley J, Wasserstein M, Rice GM, Dorenbaum A, Neuenburg JK, Musson DG, Gu Z, Sile S. (2014). Single-dose, subcutaneous recombinant phenylalanine ammonia lyase conjugated with polyethylene glycol in adult patients with phenylketonuria: an open-label, multicentre, phase 1 dose-escalation trial. Lancet. 5;384(9937):37-44. doi: 10.1016/S0140-6736(13)61841-3.